Orphan Drugs: Building the Regulatory Framework in the Czech…
A cross-industry push for better and broader access to innovative treatments is underway in the Czech Republic. Ripe for reform is the country’s…
Tagged with Rare Disease
Marco Ruggiero – General Manager, Chiesi Mexico
Chiesi Mexico’s Marco Ruggiero discusses his initial impressions of the Mexican pharma market, his strategic priorities for the affiliate, and the…
David López García – Country Manager, BioMarin Mexico
David López García, Mexico country manager of global rare genetic therapy player Biomarin, outlines the challenging situation around patient access…
Chiesi Moves into Rare Diseases & the US Market
Italian mid-cap firm Chiesi is continuing its expansion in the USA market with the launch of a Boston-based subsidiary focusing on rare and ultra-rare…
Patrik Zachar – Vice President Central Europe, Ipsen
Patrik Zachar, Vice President Central Europe of Ipsen, shares how the company has built a strong presence in oncology and neuroscience in the CE…
Karim Smaira – CEO & Kamel Ghammachi – Chairman,…
Genpharm is a Dubai-based regional company providing market access and marketing solutions for rare disease products in the MENA region. Co-Founders…
Problems Pile Up at Ipsen after Further Clinical Setback
These are worrying times for iconic French mid-cap Ipsen. Trials for palovarotene, a treatment for rare bone disorders, have been plagued by setbacks,…
Tamás Demeter – Country Manager, AOP Orphan, Hungary
Tamás Demeter, Country Manager for AOP Orphan shares his insights on the footprint of the company in Hungary, the areas of therapeutic need that AOP…
Myriam Hakim – General Manager GCC, Kyowa Kirin
Myriam Hakim, the recently appointed GM for Japanese specialty pharma firm Kyowa Kirin’s UAE affiliate, discusses the strategic significance of the…
A New Approach to Rare Diseases in Canada
Pamela Fralick of Innovative Medicines Canada (IMC) advocates for a collaborative multi-stakeholder approach to better tackle rare diseases in Canada.…
Laszlo Dinca – Managing Director, Vanessa Research, Hungary
Laszlo Dinca, managing director of Vanessa Research – Hungary, shares his insights on the company’s rare and orphan disease portfolio; the…
The UAE’s Fight Against Genetic Diseases
With a relatively high number of genetic disorders, the Arab population of the United Arab Emirates (UAE) is increasingly becoming the subject of new…
